Global Approaches for Rare Diseases and Orphan Products

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Global Approaches for Rare Diseases and Orphan Products XII. Meeting Patient and Family Needs Across the Lifespan Access to Health Care, Psychological, and Social Support Programs Anders Olauson AGRENSKA, Gothenburg EURORDIS, Paris EPF, Brussels Eesti Agrenska Foundation, Estonia

When you have a rare disease > 40 contacts Vänner BB BVC Primärvård Specialistvård Hospital Arbetsterapeut Sjukgymnast Nämnd Tjänsteman Anhöriga Grannar Social network Insurance Försäkringskasseläkare LSS Other authorities Work/ School Förskola Särskola Grundskola Bostadanpassning Hjälpmedel Arbetskamrater Skolsköterska Arbetsgivare Arbetsförmedling

In order to understand how it is to be a parent to a disabled child you have to be a parent to a disabled child yourself! Åke Martinsson, Sweden

The Family Program Needs to; Invite the whole family Have a holistic approach No shorter than 4 days Address one and the same diagnose Be part of the (Re)-hability process Offer a tailor-made program Have 4 parallel program: The child with the diagnose Parents Siblings Family related Professionals Make a documentation afterwards that has focus on the whole family

Stress and well-being among parents of children with rare diseases: a prospective intervention study: 2000-2002 The Agrenska Family program an habilitation intervension for families with children with rare diseases Lotta Dellve & Lena Samuelsson A Tallborn, L R-M Hallberg, A Fasth, M Gunnarsson, A Josefsson Nordic School of Public Health Ågrenska Sahlgrenska University Hospital Göteborg University

A mother told me. Before I came here I felt that I didn t had any influence of my life and situation, but after this program and even still after 6 month I m in charge again Before attending the family program 43 % of the mothers felt disconnected. After the family program the number was less than 7 %!

Effects families tell: Parents feel normal for the first time The family feel empowered, by meeting other in the same situation Parents get new knowledge, to take better care of their own life Children with the disorder meet other in the same situation Siblings meet other siblings Professionals meet each other

Effects scientific proof: Reduced costs for healthcare Attended family program - consumed medical care for 13.000 SEK/ year Attended ordinary program consumed for 35.000 SEK/year

Agrenska Foundation is working under the patronage of Queen Silvia of Sweden Queen Silvia inaugurates the Queen Silvia Auditorium at Agrenska Academy in 2001.

Agrenska programs Family program Adult program Respite and summer service Educations ADHD counselor Family support unit Training program to get a job Staff who has a disability Eesti Agrenska Agrenska Friends AViA

Comments from ICORD meeting in The ICORD Network. Brussels september 2007 Yes, this is something we want to see developed to pursue items of interest to us all. Patient involvement in this network should build on partnership with professionals, academia and regulators to make progress. We should also provide challenges for governments and industry to improve their policies and actions. It should develop tools for countries and regions to assist their work e.g. guides and templates for best practice, goals, and ideas or models for groups to use. The network should build and maintain good communications among us all. And lead to good involvement of patient/family groups at all levels, including research, health policy, regulatory issues, and a role for us in priority setting. AViA website can be a tool we can use

The AViA Virtual centre for research Stimulate further and deeper research regarding rare diseases Based upon experiences from Agrenska programs Holistic perspective International cross boarder cooperation's Scientific council

Educational consequences People with syndrome diagnoses often represent educational challenges

Empowerment

Broad observation instrument shows data for groups, variation within groups, differences between groups reliability considered good professor Erland Hjelmquist and docent Bengt Jansson, Göteborg University theoretical validation work remains

We want to map motor ability perception social behaviour emotional behaviour ADL language and speech learning strategies writing, reading and mathematics

Diagnoses in our database Prader Willi (13) Angelman (12) Asperger (33) Tourette (20) Achondroplasi (12) Cornelia de Lange (6) Silver Russel (6) Fragile X (30) Congenital Dystrophia Myotonica (14) Ehlers Danlos (10) Marfan (11) Turner (10) Charge (5) Möbius (2) Treacher Collins (2) 22q11 deletion/ CATCH 22 (20) PKU/ Phenylketonuria (9) Apert (1) Galactosemia (4) Klinefelter (6) Neurofibromatosis (11) Noonan (10) Osteogenesis imperfecta (2) Rubenstein Taybi (8) Sotos (11) Sturge Weber (4) Tuberos sclerosis (14) William (17) Albinism (9) Becker (7) Crouzon (7) LMBB (9) Cri du chat (10) CDG Congenital Disorders of Glycosylation (7) Hereditary spastic paraplegia (9)